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Cure Research Overview Research Terms Exon Skipping Clinical Trials Care COVID-19 Resources Newly Diagnosed Clinics Steroid Use Emergency Care Resource Library DME Guide Medical ID Bracelets Navigating School Occupational Therapy Physical Therapy For Families - Find a Physical Therapist - Pool Activities - Stretching For Physical Therapists - PT Certification - Professional Courses For Clinics Community CureDuchenne CARES CureDuchenne FUTURES CureDuchenne Champions Family Stories Events Previous Webinars Family Fundraisers About Us Mission Vision About Duchenne Blog Board of Directors Sponsors Reports and Financials Events & Webinars News Center - Press Releases - Research CD Ventures About CD Ventures Our Impact Get Involved Donate More Ways to Give Fundraise Shop Fundraising Events - Ladies Luncheon Austin - CureDuchenne Golf Shootout | Orange County, CA - Napa in Newport | Orange County, CA Search for: Donate CD Research Desktop A Cure Can't Wait CureDuchenne is funding the research to make it possible SEE THE PROGRESS With a mission to cure Duchenne muscular dystrophy CureDuchenne breaks the traditional charitable mold and balances passion with business acumen. We will fulfill our mission to cure Duchenne muscular dystrophy with our innovative venture philanthropy model that funds groundbreaking research, early diagnosis and treatment access. With pioneering education and support programs, our organization drives real change for those with living with the disease and their loved ones. The CureDuchenne one-to-one program provides meetings with our scientists, physical therapists, parents, fundraising team and family support resource coordinators. Email us at [email protected] to set up a time that works with your schedule. Together, we will cure Duchenne muscular dystrophy! Read our IMPACT Report Making an Impact on Duchenne Accelerating Curative treatments 10 Since the inception of CureDuchenne, life expectancy for Duchenne has increased by a decade. Funding Critical Clinical Trials 20 20 projects funded by CureDuchenne have progressed to clinical trials. Making an Impact $50+M We’ve raised over $50 million for research, education and care. Accelerating a Cure 1st CureDuchenne contributed early funding for the first FDA-approved Duchenne drug. Working Towards the Future $4.6B Our model has leveraged over $4.6 billion in follow-on funding for future programs from investors and biotech companies. Duchenne is a devastating muscle disease. Duchenne muscular dystrophy (DMD) is the most common form of muscular dystrophy, occurring in approximately 1:5,000 male births. Those affected with DMD lose their ability to walk, feed themselves, breathe independently and succumb to heart failure. But there’s hope through new pharmacological and gene-based therapies. You can help make a difference in finding a cure. Learn About Duchenne Message from Duchenne mom, Debra Miller Founder & CEO of CureDuchenne Receiving the diagnosis for Duchenne was the scariest time of my life and I know all about the emotions you are feeling. Equipping yourself with the knowledge you need to get the best care for your child is the best thing you can do. Connecting with other families going through the same thing can also be incredibly helpful. Once I had the confidence that I was going down the right path of care for my son, I founded the nonprofit CureDuchenne and dedicated my life to raising funds to find a cure and to helping other families navigate care and clinical trials. Consider all of us at CureDuchenne as your team that is striving to make the future better for your child. Schedule a call with our experts HERE. LATEST DUCHENNE NEWS & UPCOMING EVENTS Latest News Capricor Therapeutics recently shared an update on the FDA review August 13, 2026 The FDA will review Dyne’s application for Accelerated Approval of z-rostudirsen for skipping exon 51 July 20, 2026 Italfarmaco reports positive data from the EPIDYS trial and its ongoing open-label extension of givinostat in Duchenne July 8, 2026 Satellos reports positive interim data from adults treated with SAT-3247 July 8, 2026 FDA accepts Sarepta’s application to convert AMONDYS 45 and VYONDYS 53 from accelerated to full approval June 30, 2026 View All Latest News Upcoming Events Círculo Familiar Duchenne con CureDuchenne Zoom Reunion August 18 @ 5:00 pm WEBINAR with Dyne Therapeutics August 19 @ 10:00 am GRANDPARENTS MEET-UP: LOVE THROUGH GENERATIONS August 19 @ 12:00 pm DINNER SESSION: Westmont, NJ September 5 @ 6:00 pm VIRTUAL MEET UP: ADULT DUCHENNE CAREGIVER CONNECT SHARING THE JOURNEY September 10 @ 4:00 pm View All Events Schedule your 1:1 with our experts for personalized support HERE About Mission About Duchenne MD Blog Store News Center Get Involved Donate Fundraising Attend an Event CureDuchenne 100 Bayview Circle, Suite 5600 Newport Beach, CA 92660 (949) 872-2552 [email protected] Get Connected PRIVACY POLICY | TERMS OF USE | INDIRECT COST POLICY | TAX INFO CureDuchenne is a 501c3 registered tax-exempt nonprofit organization. Federal Tax ID: #20-0299958 | ©2026 CureDuchenne. All rights reserved. Please be advised that the contents within the CureDuchenne site include a compilation of articles, advisements, and references from the community. CureDuchenne does not provide medical advice nor is CureDuchenne a medical provider. The intent of this shared content is to serve as a point of reference for informational purposes. Please refer to your health care provider(s) for your individualized, specific care management needs. The CureDuchenne website may contain links to external websites that are not provided and/or maintained by or in any way affiliated with CureDuchenne. CureDuchenne recommends that you review the terms of service and privacy policies of these external websites before entering. Please note that CureDuchenne does not guarantee the accuracy, relevance, timeliness, or completeness of any information on these external websites. 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